Long-term Follow-up Study of Participants Following an Open Label, Multi-centre, Phase I/II Dose Escalation Trial of an Adeno-associated Virus Vector (AAV2/5-OPTIRPE65) for Gene Therapy of Adults and Children With Retinal Dystrophy Owing to Defects in RPE65 (LCA2)

Status: Completed

Phase of Trial: Phase I/II

Latest Information Update: 16 Apr 2024

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At a glance

Drugs Cevaretigene ritoparvovec (Primary)
Indications Retinal dystrophies
Focus Adverse reactions
Sponsors MeiraGTx

Most Recent Events

10 Aug 2023 Status changed from active, no longer recruiting to completed.
10 May 2023 Planned End Date changed from 1 Apr 2023 to 1 Jul 2023.
10 May 2023 Planned primary completion date changed from 1 Apr 2023 to 1 Jul 2023.

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