ASPIRO: A Phase 1/2/3, Randomized, Open-Label, Ascending-Dose, Delayed-Treatment Concurrent Control Clinical Study to Evaluate the Safety and Efficacy of AT132, an AAV8-Delivered Gene Therapy in X-Linked Myotubular Myopathy (XLMTM) Patients
Latest Information Update: 23 Aug 2024
At a glance
- Drugs Resamirigene bilparvovec (Primary)
- Indications Congenital structural myopathies; X-linked genetic disorders
- Focus Adverse reactions; First in man; Therapeutic Use
- Acronyms ASPIRO
- Sponsors Astellas Gene Therapies
- 19 Dec 2023 Planned End Date changed from 31 Oct 2030 to 31 Mar 2030.
- 01 Dec 2023 Results published in the Lancet Neurology
- 17 Nov 2023 Results published in the Genethon Media Release