Expanded Access Protocol of Patisiran for Patients With Hereditary Transthyretin-Mediated Amyloidosis (hATTR Amyloidosis) With Polyneuropathy
Latest Information Update: 22 May 2024
Price :
$35 *
At a glance
- Drugs Patisiran (Primary)
- Indications Amyloid polyneuropathy; Transthyretin-related hereditary amyloidosis
- Focus Expanded access; Therapeutic Use
- Sponsors Alnylam Pharmaceuticals
- 10 Aug 2018 Status changed from recruiting to completed.
- 25 Oct 2016 New trial record