Trial Profile

A Randomized, Controlled, Open-label, Single-ascending Dose, Phase I/II Study to Investigate the Safety and Tolerability, and Efficacy of Intravenous SGT-001 in Male Adolescents and Children With Duchenne Muscular Dystrophy

Status: Active, no longer recruiting

Phase of Trial: Phase I/II

Latest Information Update: 25 Jun 2025

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At a glance

16 Apr 2025 Primary endpoints has been amended.
16 Apr 2025 Planned End Date changed from 1 Dec 2027 to 15 Oct 2026.
16 Apr 2025 Planned primary completion date changed from 1 Dec 2026 to 15 Oct 2026.

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