Trial Profile
Intrathecal iduronidase, IV-Enzyme replacement therapy , and hematopoietic cell transplant in patients with Mucopolysaccharidosis-I (MPS-IH)
Status:
Completed
Phase of Trial:
Phase II
Latest Information Update: 16 Feb 2017
Price :
$35
*
At a glance
- Drugs Laronidase (Primary)
- Indications Mucopolysaccharidosis I
- Focus Biomarker; Pharmacodynamics
- 16 Feb 2017 New trial record
- 15 Feb 2017 Results published in the Molecular Genetics and Metabolism