Trial Profile

An Open Label, Multi-centre, Phase I/II Dose Escalation Trial of a Recombinant Adeno-associated Virus Vector (AAV2-.RPGR) for Gene Therapy of Adults and Children With X-linked Retinitis Pigmentosa Owing to Defects in Retinitis Pigmentosa GTPase Regulator (RPGR)

Status: Completed

Phase of Trial: Phase I/II

Latest Information Update: 10 Jan 2025

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At a glance

01 Nov 2024 Results assessing the safety and efficacy of AAV5-hRKp , published in the American Journal of Ophthalmology
21 Apr 2023 According to Janssen media release, updates from this study will be presented at the Association for Research in Vision and Ophthalmology (ARVO) 2023 Annual Meeting.
01 Oct 2022 Results published in the MeiraGTx Holdings Media Release.

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