Trial Profile
A phase I/II, open-label, study of intracerebral administration of adeno-associated viral vectors carrying human NaGlu cDNA for the treatment of Sanfilippo type B syndrome
Status:
Completed
Phase of Trial:
Phase I/II
Latest Information Update: 20 Dec 2019
Price :
$35
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At a glance
- Drugs AMT 110 (Primary)
- Indications Mucopolysaccharidosis III
- Focus First in man; Therapeutic Use
- 23 Sep 2017 New trial record
- 01 Sep 2017 Results published in the Lancet Neurology