Trial Profile
A Randomized, Placebo-Controlled, Crossover Study to Evaluate the Safety and Efficacy of Amifampridine Phosphate in Ambulatory Patients with Spinal Muscular Atrophy (SMA) Type 3
Status:
Completed
Phase of Trial:
Phase II
Latest Information Update: 27 Oct 2022
Price :
$35
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At a glance
- Drugs Amifampridine (Primary)
- Indications Spinal muscular atrophy
- Focus Proof of concept; Therapeutic Use
- Sponsors Catalyst Pharmaceuticals
- 01 Nov 2022 Results published in the Journal of Neurology
- 24 Oct 2022 Primary endpoint has been met. (Hammersmith Functional Motor Scale Expanded (HFMSE) Summary Statistics and Mixed Model Analysis), as per Results published in the Journal of Neurology
- 23 Jul 2020 Status changed from recruiting to completed.