Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

A Single-Center, Open-Label, Systemic Gene Delivery Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9003 Administered by Systemic Infusion in Subjects With LGMD2E (β-Sarcoglycan Deficiency)

X
Trial Profile

A Single-Center, Open-Label, Systemic Gene Delivery Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9003 Administered by Systemic Infusion in Subjects With LGMD2E (β-Sarcoglycan Deficiency)

Status: Active, no longer recruiting
Phase of Trial: Phase I/II

Latest Information Update: 16 Feb 2024

Price : $35 *
  • Adis is an information provider.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our trial profile at the time of purchase.
  • A link to download a PDF version of the trial profile will be included in your email receipt.

At a glance

  • Drugs Bidridistrogene xeboparvovec (Primary)
  • Indications Limb girdle muscular dystrophies
  • Focus Adverse reactions; First in man; Pharmacogenomic; Registrational
  • Sponsors Myonexus Therapeutics; Sarepta Therapeutics
  • Most Recent Events

    • 09 Feb 2024 Planned End Date changed from 1 Feb 2025 to 14 Feb 2027.
    • 09 Feb 2024 Planned primary completion date changed from 1 Feb 2025 to 14 Feb 2027.
    • 01 Jan 2024 Interim Post hoc exploratory analysis results assessing safety and efficacy of bidridistrogene xeboparvovec for limb-girdle muscular dystrophy published in the Nature Medicine
Subscriber content

You need to be a logged in subscriber to view this content.

If your organization has a subscription then there are several options available to help you access AdisInsight, even while working remotely.

  • IP authentication when working within your organization’s network.
  • with username/password or try via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days.
  • Contact us at AsktheExpert.AdisInsight@springer.com for assistance.

If your organization does not have a subscription to this content. To gain full access to the content and functionality of the AdisInsight database try one of the following.

  • Contact your organization’s admin about adding this content to your AdisInsight subscription
  • Buy a PDF version of the profile.
  • Request a free trial
Back to top