Trial Profile

A Post-Authorization, Multicenter, Longitudinal, Observational Safety Registry Study for Patients Treated With Voretigene Neparvovec in US

Status: Completed

Phase of Trial: Phase IV

Latest Information Update: 10 Oct 2025

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At a glance

Drugs Voretigene neparvovec (Primary)
Indications Leber congenital amaurosis; Retinal dystrophies
Focus Adverse reactions
Sponsors Spark Therapeutics

Most Recent Events

22 Sep 2025 Status changed from active, no longer recruiting to completed.
28 Sep 2020 Planned End Date changed from 1 Jan 2029 to 1 Jun 2025.
28 Sep 2020 Planned primary completion date changed from 1 Jan 2029 to 1 Jun 2025.

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