Trial Profile
An Open-label First-in-human Single Ascending Dose Study to Explore Safety, Tolerability and Efficacy of Subretinal Administration of CPK850 Gene Therapy in Patients With Retinitis Pigmentosa Due to Mutations in the Retinaldehyde Binding Protein 1 (RLBP1) Gene
Not yet recruiting
Phase of Trial:
Phase I/II
Latest Information Update: 29 Dec 2017
At a glance
- Drugs CPK-850 (Primary)
- Indications Retinitis pigmentosa
- Focus Adverse reactions; First in man; Proof of concept; Therapeutic Use
- Sponsors Novartis
- 29 Dec 2017 New trial record