Trial Profile

A Multi-Center Evaluation of the Long-Term Safety and Efficacy of Spark-sponsored Gene Therapies in Males With Hemophilia A

Status: Active, no longer recruiting

Phase of Trial: Phase I/II

Latest Information Update: 02 Dec 2024

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At a glance

Drugs Dirloctocogene samoparvovec (Primary)
Indications Haemophilia A
Focus Adverse reactions; Therapeutic Use
Sponsors NeuroRX; Spark Therapeutics

Most Recent Events

28 Nov 2024 Primary endpoint time frame changed from 4 years to 9 years, hence the protocol was amended.
19 Jan 2024 Status changed from recruiting to active, no longer recruiting.
21 Feb 2023 Planned End Date changed from 1 Dec 2022 to 1 Dec 2032.

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