Trial Profile
Phase 2 Active Treatment Study to Evaluate the Efficacy and Safety of SRK-015 in Patients With Later-Onset Spinal Muscular Atrophy (TOPAZ)
Status:
Completed
Phase of Trial:
Phase II
Latest Information Update: 19 Apr 2024
Price :
$35
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At a glance
- Drugs Apitegromab (Primary)
- Indications Spinal muscular atrophy
- Focus Proof of concept; Therapeutic Use
- Acronyms TOPAZ
- Sponsors Scholar Rock
- 22 Apr 2024 Status changed from active, no longer recruiting to completed.
- 20 Mar 2024 This trial has been completed in Netherlands, according to European Clinical Trials Database record.
- 19 Mar 2024 According to the Scholar Rock media release, 12-month data from Phase 2 TOPAZ trial presented at American academy of Neurology 2024.