Acceptability study of a new paediatric formulation of Orphacol (cholic acid) in paediatric patients treated for inborn errors in primary bile acid synthesis due to 3ß-Hydroxy-5-C27- steroid oxidoreductase deficiency or 4-3-Oxosteroid-5ß-reductase deficiency-ORPH-PAED-01
Latest Information Update: 30 Jul 2018
At a glance
- Drugs Cholic acid (Primary)
- Indications Inborn genetic disorders; Liver disorders
- Focus Therapeutic Use
- Acronyms ORPH-PAED-01
Most Recent Events
- 30 Jul 2018 Status changed from active, no longer recruiting to completed.
- 22 Jun 2018 New trial record