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A supplemental clinical trial of AT-GAA in pediatric Pompe patients

Trial Profile

A supplemental clinical trial of AT-GAA in pediatric Pompe patients

Status: Planning
Phase of Trial: Phase I

Latest Information Update: 03 Jul 2018

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At a glance

  • Drugs Cipaglucosidase alfa (Primary)
  • Indications Glycogen storage disease type II
  • Focus Adverse reactions
  • Most Recent Events

    • 03 Jul 2018 New trial record
    • 26 Jun 2018 According to an Amicus Therapeutics media release, the design of this study has been discussed with the Scientific Advice Working Party (SAWP) within the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA).
    • 26 Jun 2018 According to an Amicus Therapeutics media release, this study is expected to start in 2019.
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