An second Expanded access study of RT001 in patient with Infantile Neuroaxonal Dystrophy (INAD)
Latest Information Update: 23 Oct 2018
At a glance
- Drugs RT 001 (Primary)
- Indications Neuroaxonal dystrophies
- Focus Expanded access; Therapeutic Use
- Sponsors Retrotope
- 15 Oct 2018 According to a Retrotope media release, data from 2 patients enrolled in an expanded access program were presented at the 2018 National Organization for Rare Disorders (NORD) Rare Diseases & Orphan Products Breakthrough Summit.
- 10 Jul 2018 New trial record