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An second Expanded access study of RT001 in patient with Infantile Neuroaxonal Dystrophy (INAD)

Trial Profile

An second Expanded access study of RT001 in patient with Infantile Neuroaxonal Dystrophy (INAD)

Status: Active, no longer recruiting
Phase of Trial: Clinical Phase Unknown

Latest Information Update: 23 Oct 2018

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At a glance

  • Drugs RT 001 (Primary)
  • Indications Neuroaxonal dystrophies
  • Focus Expanded access; Therapeutic Use
  • Sponsors Retrotope
  • Most Recent Events

    • 15 Oct 2018 According to a Retrotope media release, data from 2 patients enrolled in an expanded access program were presented at the 2018 National Organization for Rare Disorders (NORD) Rare Diseases & Orphan Products Breakthrough Summit.
    • 10 Jul 2018 New trial record
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