Mucopolysaccharidosis VII Disease Monitoring Program (MPS VII DMP)
Latest Information Update: 22 Jun 2026
At a glance
- Drugs Vestronidase alfa (Primary)
- Indications Mucopolysaccharidosis VII
- Focus Adverse reactions; Therapeutic Use
- Acronyms MPS VII DMP
- Sponsors Ultragenyx Pharmaceutical
Most Recent Events
- 11 Jun 2026 Planned End Date changed from 1 May 2033 to 1 Apr 2032.
- 11 Jun 2026 Planned primary completion date changed from 1 May 2033 to 1 Apr 2032.
- 10 Oct 2022 Planned number of patients changed from 35 to 50.