Lentiviral Gene Transfer for Treatment of Children Older Than 2 Years of Age With X-Linked Severe Combined Immunodeficiency
Latest Information Update: 06 Dec 2022
At a glance
- Drugs MB 107 (Primary) ; Busulfan; Palifermin
- Indications Immunodeficiency disorders
- Focus Adverse reactions; Pharmacogenomic; Therapeutic Use
- Acronyms LVXSCID-OC
- 06 Nov 2019 According to a Mustang Bio media release, data will be presented at 61st American Society of Hematology Annual Meeting.
- 22 Aug 2018 New trial record