Trial Profile

Lentiviral Gene Transfer for Treatment of Children Older Than 2 Years of Age With X-Linked Severe Combined Immunodeficiency

Status: Recruiting

Phase of Trial: Phase I/II

Latest Information Update: 20 Jun 2025

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At a glance

Drugs MB 107 (Primary) ; Busulfan; Palifermin
Indications Immunodeficiency disorders; X-linked genetic disorders
Focus Pharmacogenomic; Therapeutic Use

Most Recent Events

08 Mar 2024 Planned End Date changed from 31 Dec 2024 to 31 Dec 2032.
08 Mar 2024 Planned primary completion date changed from 31 Dec 2024 to 31 Dec 2032.
27 Jan 2024 Planned number of patients changed from 30 to 40.

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