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A phase 1/2 study of AVR-RD-04 for the treatment of patients with cystinosis

Trial Profile

A phase 1/2 study of AVR-RD-04 for the treatment of patients with cystinosis

Planning
Phase of Trial: Phase I/II

Latest Information Update: 18 Jan 2019

At a glance

  • Drugs AVR-RD-04 (Primary)
  • Indications Cystinosis
  • Focus Adverse reactions; Therapeutic Use
  • Most Recent Events

    • 18 Jan 2019 According to an AVROBIO media release, the US FDA has accepted the IND application to initiate this study. This study will be under the direction of the Dr. Stephanie Cherqui, PhD, Associate Professor in the Department of Pediatrics at UCSD.
    • 23 Aug 2018 New trial record
    • 09 Aug 2018 According to an AVROBIO media release, this University of California, San Diego sponsored study remains on track to enrol the first patient in 2019.
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