Trial Profile

A Randomized, Double-Blind, Placebo-Controlled, Multi-Center Study to Evaluate the Efficacy of ManNAc in Subjects With GNE Myopathy

Status: Active, no longer recruiting

Phase of Trial: Phase II

Latest Information Update: 18 Jun 2025

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At a glance

Drugs N acetyl D mannosamine (Primary)
Indications Nonaka distal myopathy
Focus Therapeutic Use
Acronyms MAGiNE

Most Recent Events

13 Jun 2025 Planned primary completion date changed from 28 May 2025 to 27 Jun 2025.
17 Oct 2024 Planned End Date changed from 15 Jul 2024 to 30 Oct 2025.
17 Oct 2024 Planned primary completion date changed from 28 Mar 2024 to 28 May 2025.

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