Trial Profile

Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for Sickle Cell Disease

Status: Active, no longer recruiting

Phase of Trial: Phase I

Latest Information Update: 18 Jul 2024

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At a glance

Drugs BCL11a shRNA(miR) (Primary) ; Busulfan
Indications Sickle cell anaemia
Focus Therapeutic Use

Most Recent Events

09 Jul 2024 Planned End Date changed from 13 Nov 2024 to 13 Dec 2024.
09 Jul 2024 Planned primary completion date changed from 13 Aug 2024 to 13 Sep 2024.
11 Jun 2024 Planned primary completion date changed from 13 May 2024 to 13 Aug 2024.

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