A pivotal randomized clinical trial of IB-1000 for Niemann-Pick-disease-type-C
Latest Information Update: 25 Nov 2018
At a glance
- Drugs Acetylleucine (Primary)
- Indications Niemann-Pick disease type C
- Focus Registrational; Therapeutic Use
- Sponsors IntraBio
Most Recent Events
- 25 Nov 2018 New trial record