A pivotal randomized clinical trial of IB-1000 for Late-Onset Tay Sachs (LOTS) disease
Latest Information Update: 26 Nov 2018
At a glance
- Drugs Acetylleucine (Primary)
- Indications Tay-Sachs disease
- Focus Registrational; Therapeutic Use
Most Recent Events
- 26 Nov 2018 New trial record