Trial Profile

Effects of N-Acetyl-L-Leucine on Niemann Pick Type C Disease: A Multinational, Multicenter, Open-label, Rater-blinded Phase II Study

Status: Completed

Phase of Trial: Phase II

Latest Information Update: 01 Dec 2023

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At a glance

Drugs Levacetylleucine (Primary)
Indications Niemann-Pick disease type C
Focus Therapeutic Use
Sponsors IntraBio

Most Recent Events

05 Oct 2023 This trial has been completed in Slovakia (End Date: 07 Nov 2022), according to the European Clinical Trials Database record.
29 Jun 2023 According to IntraBio media release,Based on these positive trials, IntraBio will proceed with global regulatory submissions to the United States Food and Drug Administration (FDA), the European Medicines Agency (EMA), and other global regulators.
20 Feb 2023 This trial has been completed in Germany (End Date: 7 Nov 2022), according to European Clinical Trials Database record.

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