Trial Profile

A Global, Multicenter, Single-arm, Matched External Control Study of Intrathecal SHP611 in Subjects With Late Infantile Metachromatic Leukodystrophy

Status: Active, no longer recruiting

Phase of Trial: Phase II

Latest Information Update: 21 Oct 2025

Price :

$35 ^*

Note:

Adis is an information provider.
Final gross price and currency may vary according to local VAT and billing address.
Your purchase entitles you to full access to the information contained in our trial profile at the time of purchase.
A link to download a PDF version of the trial profile will be included in your email receipt.

At a glance

Drugs Cerebroside-sulfatase (Primary)
Indications Metachromatic leukodystrophy
Focus Therapeutic Use
Acronyms Embolden
Sponsors Shire; Shire Human Genetic Therapies

Most Recent Events

16 Oct 2025 Planned End Date changed from 31 Oct 2025 to 31 Jan 2026.
07 Mar 2025 Planned End Date changed from 6 Mar 2025 to 31 Oct 2025.
13 Dec 2022 Planned primary completion date changed from 2 Mar 2023 to 9 Mar 2023.

You need to be a logged in or subscribed to view this content

If your organization or you do not have a subscription, try one of the following:

Contacting your organization’s admin about adding this content to your AdisInsight subscription
Buying a PDF version of any individual profile
Request a free trial (opens in a new window)

If your organization has a subscription, there are several access options, even while working remotely:

Working within your organization’s network
Login with username/password or try to access via your institution
Persisted access using your organization’s identifier stored in your user browser for 90 days

For assistance, contact us at asktheexpert.adisinsight@springer.com