Expanded Access to Triheptanoin
Latest Information Update: 14 Jan 2025
At a glance
- Drugs Triheptanoin (Primary) ; Triheptanoin (Primary)
- Indications De Vivo disease; Lipid metabolism disorders
- Focus Expanded access; Therapeutic Use
- Acronyms UX007-EAP101
- Sponsors Ultragenyx Pharmaceutical
- 19 Dec 2018 New trial record