Named Patient or Compassionate Use for Treatment Use of ATB200/AT2221 for Patients With Pompe Disease
Latest Information Update: 20 Aug 2024
At a glance
- Drugs Cipaglucosidase alfa (Primary)
- Indications Glycogen storage disease type II
- Focus Expanded access; Therapeutic Use
- Sponsors Amicus Therapeutics
Most Recent Events
- 11 Mar 2019 New trial record