Physician Initiated Expanded Access Request for Treatment Use of Migalastat Hydrochloride (AT1001), an Investigational Treatment for Individual Patients With Fabry Disease (AT1001-188)
Latest Information Update: 14 May 2025
At a glance
- Drugs Migalastat (Primary)
- Indications Fabry's disease
- Focus Expanded access; Therapeutic Use
- Sponsors Amicus Therapeutics
Most Recent Events
- 19 Mar 2019 New trial record