Trial Profile

An Open-label Study of the Safety, Pharmacokinetics, Efficacy, Pharmacodynamics, and Immunogenicity of Cipaglucosidase Alfa/Miglustat in Pediatric Subjects Aged 0 to < 18 Years With Late-onset Pompe Disease

Status: Active, no longer recruiting

Phase of Trial: Phase III

Latest Information Update: 30 Oct 2025

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At a glance

27 Oct 2025 Status changed from recruiting to active, no longer recruiting.
19 Oct 2021 Planned End Date changed from 1 Sep 2021 to 1 Jun 2026.
19 Oct 2021 Planned primary completion date changed from 1 Sep 2021 to 1 Jun 2026.

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