Trial Profile

A Phase I Clinical Trial for Gene Therapy in Infantile Malignant Osteopetrosis (IMO) to Evaluate the Safety and Preliminary Efficacy of Autologous CD34+ Enriched Cells Transduced With a LV Vector Encoding the TCIRG1 Gene

Status: Discontinued

Phase of Trial: Phase I

Latest Information Update: 15 Jul 2022

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At a glance

11 Jul 2022 Status changed from active, no longer recruiting to discontinued due to feasibility.
03 Nov 2021 According to a Rocket Pharmaceuticals media release, clinical update is anticipated later in Q4 2021.
20 Aug 2021 Status changed from suspended to active, no longer recruiting.

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