An expanded access study of SLS-005 (Trehalose) for Sanfilippo Syndrome
Latest Information Update: 19 Jul 2019
At a glance
- Drugs Trehalose (Primary)
- Indications Mucopolysaccharidosis III
- Focus Expanded access; Therapeutic Use
Most Recent Events
- 15 Jul 2019 According to a Seelos Therapeutics media release, Team Sanfilippo Foundation (TSF) and Seelos Therapeutics will continue to work aggressively to raise additional funds to accommodate as many children as possible into this expanded access program.
- 15 Jul 2019 According to a Seelos Therapeutics media release, Seelos announced today the receipt of a grant from Team Sanfilippo Foundation.The grant will be used towards the funding of the FDA/EMA Open-Label Phase IIb/III Study in Sanfilippo Syndrome type A and B (CT Profile: 304671) and this separate expanded access study for Sanfilippo type C and D as well as type A and B patients who do not meet the trial entry criteria (CT profile 307744).
- 06 Jun 2019 According to a Seelos Therapeutics media release, Dr. Wasiewski will lead the collaboration with Team Sanfilippo Foundation (TSF) to spearhead this trial.