Trial Profile

A Long-Term Follow-up Study to Evaluate the Safety and Efficacy of Adeno Associated Virus (AAV) Serotype 8 (AAV8)-Mediated Gene Transfer of Glucose-6-Phosphatase (G6Pase) in Adults with Glycogen Storage Disease Type Ia (GSDIa)

Status: Completed

Phase of Trial: Phase II

Latest Information Update: 10 Mar 2025

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At a glance

06 Mar 2025 Status changed from active, no longer recruiting to completed.
21 Apr 2023 Planned End Date changed from 1 Dec 2025 to 1 Dec 2026.
21 Apr 2023 Planned primary completion date changed from 1 Dec 2025 to 1 Dec 2026.

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