A Phase 2, Two-Part, Multiple-Ascending-Dose Study of SRP-5051 for Dose Determination, Then Dose Expansion, in Patients With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatment
Latest Information Update: 12 Mar 2025
At a glance
- Drugs SRP-5051 (Primary)
- Indications Duchenne muscular dystrophy
- Focus Adverse reactions; Proof of concept; Registrational; Therapeutic Use
- Acronyms MOMENTUM
- Sponsors Sarepta Therapeutics
Most Recent Events
- 10 Mar 2025 Status changed from active, no longer recruiting to discontinued.
- 29 Jan 2024 According to a Sarepta Therapeutics media release, Eugenio Mercuri M.D., Ph.D., head of the Neuromuscular Unit, Catholic University, Rome, Italy, is an investigator in the study.
- 29 Jan 2024 Results (till date; High Dose and Low dose results at 28 weeks) published in a Sarepta Therapeutics media release.