A Multicenter, Multinational, Open-Label Extension Study of Recombinant Human N-acetylgalactosamine 4-sulfatase (rhASB) in Patients with Mucopolysaccharidosis VI
Latest Information Update: 22 Jul 2019
At a glance
- Drugs Galsulfase (Primary)
- Indications Mucopolysaccharidosis IV
- Focus Registrational; Therapeutic Use
- Acronyms Aryplase Phase 3 Open-Label Extension
- Sponsors BioMarin Pharmaceutical
- 22 Jul 2019 New trial record