A Phase 3, Multicenter, Randomized, Double-Blind, Placebo-controlled Study to Evaluate the Safety and Efficacy of Phenoptin 20 mg/kg/day to Increase Phenylalanine Tolerance in Phenylketonuric Children on a Phenylalanine-restricted Diet
Latest Information Update: 03 Aug 2022
At a glance
- Drugs Sapropterin (Primary)
- Indications Phenylketonuria
- Focus Registrational; Therapeutic Use
- Sponsors BioMarin Pharmaceutical
Most Recent Events
- 08 Aug 2019 New trial record