An Observational Long-term Follow-up Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency (ADA-SCID)
Latest Information Update: 13 Apr 2022
At a glance
- Drugs Simoladagene autotemcel (Primary)
- Indications Adenosine deaminase deficiency
- Focus Adverse reactions; Therapeutic Use
- Sponsors Orchard Therapeutics
Most Recent Events
- 09 Aug 2019 New trial record