A Phase 2a, Randomized, Open-Label Study to Evaluate the Efficacy, Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ISIS 702843 Administered Subcutaneously to Patients With Non-Transfusion Dependent β-Thalassemia Intermedia
Latest Information Update: 24 Feb 2025
At a glance
- Drugs Sapablursen (Primary)
- Indications Beta-thalassaemia
- Focus Therapeutic Use
- Sponsors Ionis Pharmaceuticals
Most Recent Events
- 16 Apr 2024 This trial has been completed in Greece (End date: 2023-03-28) according to European Clinical Trials Database record.
- 28 Apr 2023 Status changed from active, no longer recruiting to discontinued.
- 03 Jan 2022 Status changed from recruiting to active, no longer recruiting.