Trial Profile

A 40-Week, Open-label Extension Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome

Status: Completed

Phase of Trial: Phase III

Latest Information Update: 07 Mar 2025

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At a glance

Drugs Trofinetide (Primary) ; Trofinetide (Primary)
Indications Rett syndrome
Focus Adverse reactions
Acronyms LILAC-1; LILAC™
Sponsors Acadia Pharmaceuticals

Most Recent Events

05 Mar 2025 According to an Acadia Pharmaceuticals media release, results of DAFFODIL, LAVENDER, LILAC-1 and LILAC-2 studies supported the FDA approval of DAYBUE in adults and pediatric patients two years of age or older.
18 Jul 2024 According to Acadia media release, data from this trial published in journal Med
18 Jul 2024 Results published in the Acadia Media Release

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