Nonsense Mutation Aniridia: An Ataluren (PTC124) Phase 2 Extension Study
Latest Information Update: 10 Oct 2019
Price :
$35 *
At a glance
- Drugs Ataluren (Primary)
- Indications Aniridia
- Focus Adverse reactions
- Sponsors PTC Therapeutics
- 10 Oct 2019 New trial record