Safety and efficacy of nitisinone in patients with tyrosinemia type 1 disease: A retrospective multicentric observational study
Latest Information Update: 30 Oct 2019
At a glance
- Drugs Nitisinone (Primary)
- Indications Tyrosinaemia type I
- Focus Adverse reactions; Pharmacodynamics; Therapeutic Use
Most Recent Events
- 30 Oct 2019 New trial record
- 01 Sep 2019 Results published in the Medicine