A Single Arm, Open Label Clinical Study to Enable Process Validation of Commercial Grade Ex Vivo Hematopoietic Stem Cell Gene Therapy (OTL-101) in Subjects With Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency (ADA-SCID)
Latest Information Update: 08 Aug 2022
At a glance
- Drugs Simoladagene autotemcel (Primary)
- Indications Adenosine deaminase deficiency
- Focus Registrational; Therapeutic Use
- Sponsors Orchard Therapeutics
Most Recent Events
- 01 Aug 2022 Planned End Date changed from 28 Feb 2022 to 30 Aug 2021.
- 01 Aug 2022 Status changed from suspended to discontinued as enrollment is on hold due to business reasons. Study will not be performed.
- 01 Oct 2020 Planned End Date changed from 28 Feb 2021 to 28 Feb 2022.