A Long-term Follow-up Study of Patients with MPS IIIB from Gene Therapy Clinical Trials Involving the Administration of ABO-101 (rAAV9.CMV.hNAGLU)
Latest Information Update: 01 Jun 2022
At a glance
- Drugs ABO-101 (Primary)
- Indications Mucopolysaccharidosis III
- Focus Adverse reactions
- Sponsors Abeona therapeutics
- 25 May 2022 Status changed from recruiting to discontinued.
- 21 Apr 2022 This trial has been discontinued in Germany, according to European Clinical Trials Database record.
- 17 Feb 2021 Status changed from not yet recruiting to recruiting.