Evaluate the Long Term Effectiveness & Safety of the Use of Carglumic Acid (Carbaglu®) in Patients With Propionic Acidemia (PA) or Methylmalonic Acidemia (MMA).
Latest Information Update: 24 Mar 2025
At a glance
- Drugs Carglumic acid (Primary) ; Cobalamin; Levocarnitine; Metronidazole
- Indications Hyperammonaemia
- Focus Therapeutic Use
Most Recent Events
- 16 Mar 2025 Status changed from recruiting to completed.
- 28 Feb 2020 New trial record