Expanded Use Of Recombinant Human Acid Alpha-Glucosidase/N-butyl-deoxynojirimycin (ATB200/AT2221) For Patients With Infantile-Onset Pompe Disease
Latest Information Update: 04 Nov 2021
At a glance
- Drugs Cipaglucosidase alfa (Primary) ; Miglustat (Primary)
- Indications Glycogen storage disease type II
- Focus Expanded access; Therapeutic Use
- Sponsors Amicus Therapeutics
Most Recent Events
- 03 Apr 2020 New trial record