Evaluation of safety and efficacy in mitapivat sulfate in adult patients with sickle cell disease
Latest Information Update: 21 May 2025
At a glance
- Drugs Mitapivat (Primary)
- Indications Sickle cell anaemia
- Focus Adverse reactions; Proof of concept; Therapeutic Use
- Acronyms ESTIMATE
Most Recent Events
- 14 May 2025 According to an Agios Pharmaceuticals Media Release, data from this study will be featured during the 30th European Hematology Association (EHA) Congress (EHA 2025) in Milan, Italy, June 12-15, 2025.
- 12 Dec 2023 Results of the safety and efficacy of treatment with mitapivat in patients with SCD from the 1-year fixed-dose extension period , presented at the 65th American Society of Hematology Annual Meeting and Exposition
- 15 Jun 2023 Results (n=9) assessing pre-specified safety and efficacy data of the 1-year fixed-dose extension period (FDEP) ofmitapivat treatment in subjects with SCD, presented at the 28th Congress of the European Haematology Association.