An Open-label, Phase 1/2 Trial of Gene Therapy 4D-125 in Males With X-linked Retinitis Pigmentosa (XLRP) Caused by Mutations in the RPGR Gene
Latest Information Update: 23 Mar 2025
At a glance
- Drugs 4D 125 (Primary)
- Indications Retinitis pigmentosa
- Focus Adverse reactions; First in man; Proof of concept
- Sponsors 4D Molecular Therapeutics
Most Recent Events
- 13 Nov 2024 According to a 4D Molecular Therapeutics media release, Program updates expected in early January 2025.
- 08 Aug 2024 According to a 4D Molecular Therapeutics media release,Program updates expected in Q4 2024.
- 09 Jan 2023 According to a 4D Molecular Therapeutics media release, enrollment in this phase 1/2 study has been completed in the fourth quarter of 2022. The company will continue to follow these patients for 24 months and anticipate clinical data updates in 2024.