Trial Profile

An Extension Study of JR-171-101 Study in Patients With Mucopolysaccharidosis Type I

Status: Active, no longer recruiting

Phase of Trial: Phase I/II

Latest Information Update: 23 May 2025

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At a glance

Drugs Lepunafusp alfa (Primary)
Indications Mucopolysaccharidosis I
Focus Adverse reactions
Sponsors JCR Pharmaceuticals

Most Recent Events

16 May 2025 Planned End Date changed from 30 Apr 2025 to 31 May 2025.
05 Sep 2024 Results presented in the JCR Pharmaceuticals media release.
05 Sep 2024 According to a JCR Pharmaceuticals media release, data from this study presented at SSIEM Annual Symposium 2024.

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