Trial Profile

An Extension Study of JR-171-101 Study in Patients With Mucopolysaccharidosis Type I

Status: Completed

Phase of Trial: Phase I/II

Latest Information Update: 01 Oct 2025

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At a glance

Drugs Lepunafusp alfa (Primary)
Indications Mucopolysaccharidosis I
Focus Adverse reactions
Sponsors JCR Pharmaceuticals

Most Recent Events

28 Aug 2025 Status changed from active, no longer recruiting to completed.
16 May 2025 Planned End Date changed from 30 Apr 2025 to 31 May 2025.
05 Sep 2024 Results presented in the JCR Pharmaceuticals media release.

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